The Efficacy and Systemic Safety of a Novel Once-a-Day Timolol 0.1% Gel Formulation. The Benefits of Improved Drug Vehicle

H Uusitalo1 MD, M Kähönen2 MD, A Ropo3 MD, and V Turjanmaa2 MD

Departments of 1Ophthalmology and 2Clinical Physiology, Tampere University Hospital, Finland and 3Santen Oy, Clinical Research, Finland

Purpose: To evaluate the efficacy and systemic side effects of a novel once-a-day timolol 0.1% eye gel (Nyolol Gel®, Nyogel 0.1%®, Timosan®) formulated with an innovative mucoadhesive vehicle, containing a combination of carbomer and PVA, with a traditional timolol 0.5% solution.

Method: A phase I, randomised, double-masked, two-period, two-week, cross-over study in 24 healthy volunteers. The tests used: measurement of IOP; aqueous humour flow; exercise test (ergometry); analyses of haemodynamic characteristics and pulmonary function test; plasma concentration of timolol.

Results: Aqueous timolol 0.5% decreased peak heart rate in exercise test by 19,0 beats/min, which was statistically significant from the reduction of only 4,6 beats/min for the timolol 0.1% gel group. The two formulations differed significantly also in their capability to change haemodynamic parameters in rest. The novel mucoadhesive gel formulation did not change these parameters whereas the aqueous solution was seen to decrease heart rate and the heamodynamic response to body position. The maximum plasma concentration of timolol was about 10 fold lower after timolol 0.1% gel as compared to aqueous timolol 0.5%. There was no statistical difference between the once-a-day timolol 0.1% gel and the traditional twice-a-day timolol 0.5% solution in their capability to decrease IOP or aqueous humour production.

Conclusions: The results indicate that by using a mucoadhesive vehicle that enhances timolol’s corneal penetrability, it is possible to 1) reduce the concentration of active timolol to 0.1% while maintaining its IOP-lowering efficacy; 2) to reduce the applications to only once daily; 3) to improve the efficacy/systemic side effect ratio. The present type of test pattern is a valuable tool when new drugs and formulations are designed.